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RNA interference
Alternative splicing
Neuromuscular junction
Mechanotransduction
Heart failure
Cardiomyopathy
Muscle regeneration
Mice
Glutamate
Rare neuromuscular diseases
Astrocyte
Neuromuscular diseases
DMD
Gene therapy
Animals
Antisense oligonucleotides
Myotonic dystrophy
Autoimmune diseases
Dystrophin
COVID-19
Heart
Thérapie génique
Motoneuron
PABPN1
AAV
MBNL
Cancer
Becker muscular dystrophy
Congenital myopathy
Outcome measures
Dermatomyositis
Congenital muscular dystrophy
Humans
Genotype phenotype correlation
Clinical trials
Satellite cell
Transcriptomics
Myasthenia gravis
Autophagy
Laminopathie
Lamin A/C
Myopathy
FSHD
Cytokines
CMS
Treatment
Nuclear envelope
Laminopathy
Cell therapy
Myopathies
Laminopathies
Duchenne muscular dystrophy
Actin
Calcium
Muscle
Neuromuscular disease
Mouse model
Fabry disease
Muscular dystrophy
Myotonic Dystrophy type 1
Errance diagnostique
Myoblasts
OPMD
Myotonic Dystrophy
Myogenesis
Cytoskeleton
Therapy
Autoimmunity
Long read sequencing
Centronuclear myopathy
Biomarker
Autoantibodies
Skeletal muscle
CRISPRi
Aged
Dynamin 2
CTG repeat contractions
Myositis
Rare diseases
Inflammation
Myotonic dystrophy type 1
Brain
ALS
LMNA gene
Thymus
RNA biology
Exercise
Satellite cells
Regeneration
Amyotrophic lateral sclerosis
Aging
Transgenic mouse model
Trinucleotide repeat expansion
Biomarkers
Fibrosis
Myasthenia Gravis MG
Male
LMNA
Lamin A/C LMNA gene
Dilated cardiomyopathy